Upcoming Events

Clinical Development of Gene Therapy Products for Rare Diseases

The FDA’s Center for Biologics Evaluation and Research (CBER) Office of Tissues and Advanced Therapies (OTAT) is hosting a virtual town hall to answer stakeholder questions related to the clinical […]

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CIDD San Antonio Drug Discovery Symposium

Keynote Speaker: Dr. John LaMattina, Senior Partner at PureTech Health and Former President of Research and Development, Pfizer "Pharna & Profits - Balancing Innovation, Medicine and Drug Prices"

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2023 ASPET Guppy Tank Translational Science Pitch Competition

The “Guppy Tank” competition will showcase translational science pitches from four young scientists who will be coached by mentors with established experience in the biotech, pharma, and entrepreneurship realms. In […]

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St. Louis Union Station Hotel, 1820 Market St.
St. Louis, Missouri 63103 United States
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OTAT Town Hall: Clinical Development of Gene Therapy Products for Rare Diseases

The FDA’s Center for Biologics Evaluation and Research (CBER) Office of Tissues and Advanced Therapies (OTAT) is hosting a virtual town hall to answer stakeholder questions related to the clinical development of gene therapy products for rare diseases (excluding hematology/oncology products). This event is part of a series to answer questions from stakeholders about a variety of topics on which OTAT has regulatory oversight.

FOCUS FOR THIS TOWN HALL: GENE THERAPY PRODUCTS INTENDED TO TREAT RARE DISEASES

There are around 7,000 known rare diseases affecting more than 30 million people in the United States. Many rare diseases are life-threatening, and only a fraction of rare diseases have an available treatment. Developing safe and effective gene therapy products to treat rare diseases can be challenging; despite these challenges, gene therapy-related research and development continue to grow rapidly. To support continued growth in the gene therapy field, FDA developed a guidance document in January 2020 to provide recommendations to sponsors developing gene therapy products intended to treat rare diseases.

MEETING LOGISTICS

  • Date: Tuesday, February 7, 2023
  • Time: 11:30 a.m. to 1:00 p.m. ET
  • Location: The webinar will be held via Zoom.
  • Registration: Registration is required. Please register for the event now by clicking the button below.

Register Here

2023 ASPET Guppy Tank Translational Science Pitch Competition

The “Guppy Tank” competition will showcase translational science pitches from four young scientists who will be coached by mentors with established experience in the biotech, pharma, and entrepreneurship realms. In addition, the Guppy Tank event will feature a keynote discussion by Dr. Trivia Frazier (President and CEO of Obatala Sciences) who will highlight the importance of a translational vision to scientific innovations and effective strategies for a successful science pitch. This session will be an exciting and essential educational opportunity for young scientists to hone their translational scientific communication skills while getting publicly recognized for their talents.

View Flyer Here

Please use the link below to fill out the application by January 6th.

www.aspet.org/guppytank2023

If you have any questions, please do not hesitate to reach out to Khalid Garman (khalid.garman@nih.gov) or Saranya Radhakrishnan (sara.radkrish@gmail.com)

Previous Events

IDDD Roundtable Workshop: Greater Houston Area Collaborative Biomedical Breakthrough Resources

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IDDD Roundtable Workshop

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Foundations of Cancer Therapeutics: Commercialization

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IDDD Round Table Workshop: 3rd Annual COVID/Vaccine Update

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TexSyn V Synthetic Chemistry in Texas

University of Houston Guest Speakers Professor Richmond SarpongUniversity of California, BerkeleyDr. Jennifer Albaneze-WalkerLeader, Separations and Technologies Group, Bristol-Myers SquibbProfessor Greg CunyUniversity of HoustonProfessor Kami HullUniversity of Texas, Austin Professor Junha […]

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GCC IDDD Conference

GCC Innovative Drug Discovery and Development Conference Accelerating Drug Development – Learning from Success and Failure Confirmed Speakers: Regina Barzilay, MIT; Andrea Carfi, Moderna; Rima Chakrabarti, KdT Ventures; Klaus Hoeflich, Nested Therapeutics; Donna Huryn, U. […]

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IDDD Round Table Workshop: Developing Therapeutics for Neurodegenerative Diseases

This workshop will feature presentations from Jim Ray, PhD, MD Anderson Cancer Center and Zachary Sweeney, PhD, CEO, Interline Therapeutics. The workshop will take place in-person (pending pandemic) at the BioScience Research […]

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IDDD Roundtable Workshop: SARS-CoV-2 Vaccine Update and Future Prospects

This workshop will be the 1 year follow up with Drs. Alan Barrett and Roger Nosal to discuss what has transpired over the course of the last year and what we can expect in the […]

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2nd Annual Innovative Drug Discovery and Development Conference

Please save the date for this exciting conference and stay tuned for speaker updates.  James Inglese, NIH/NCATS is confirmed. More information can be found on the conference website.

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Bioscience Research Collaborative (BRC), 6500 Main Street, Auditorium
Houston, TX 77030 United States
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For speaker videos and slides, Click Here.